Javed Shaikh, Director of RWE & HEOR, Axtria, explains how harnessing next-generation sequencing and AI-powered analytics ...

Discover how an emerging technology called tRNA therapy could become the next big thing in genetic disease treatment.

Marks’ resignation leaves the field without a regulator many view as “integral” to its progress over the last decade.

The firm plans to use improvement in left ventricular mass index and increased frataxin protein expression after LX2006 treatment as co-primary endpoints.

Industry updates and investment insights—including investor behavior and fundraising advice—were among the topics experts ...