After months of uncertainty and controversy, the FDA has given approval to Sarepta's Duchenne muscular dystrophy drug – even though it hasn't yet shown any proof it can slow progress of the ...

She knew instantly that Charley had Duchenne muscular dystrophy (DMD ... One of the symptoms is enlarged calf muscles because the muscle tissue is abnormal and may contain scar tissue, according ...

A new study led by researchers at the Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

This is the metadata section. Skip to content viewer section. This case study introduces students to Duchenne muscular dystrophy (DMD) and its underlying genetics, cell biology, and some of the ...

Duchenne muscular dystrophy (DMD) is the most common genetic muscle disorder ... Adeno-associated viral 'packages' carrying truncated dystrophin genes were injected into the calf muscle of mice unable ...

Congestive heart failure or irregular heart rhythms (arrhythmias) occur in all people with Duchenne muscular dystrophy by age 18. Chest and back deformities (scoliosis). Enlargement of the calf ...

Suneel Ram’s needs gradually became greater after he was diagnosed at age 3 with Duchenne muscular dystrophy, a muscle-wasting genetic disorder that afflicts one in 5,000 boys. Today ...

Duchenne muscular dystrophy (DMD) is perhaps the best known of the congenital muscular dystrophies. It is an X-linked disorder that is invariably progressive and fatal, affecting 1 in 3500 newborn ...