The CHMP recommends conditional marketing authorization for Duvyzat to treat Duchenne muscular dystrophy in patients aged 6 ...

While right-wing populism surges in some of the world’s leading democracies, Chile’s leftist government is rushing in the ...

A community has come together to surprise 9-year-old Killian Bauer who is living with Duchenne muscular dystrophy, with a brand new wheelchair accessible van. 35,048 people played the daily ...

Gene therapy has emerged as a promising approach to previously untreatable conditions, including Duchenne muscular dystrophy (DMD), a progressive disorder caused by DMD mutations that leads to early ...

A new study led by researchers at Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

Italfarmaco's oral HDAC inhibitor Duvyzat has been recommended for approval in the EU as a treatment for Duchenne muscular dystrophy (DMD), setting it on course to become the first non-steroidal ...

A new study led by researchers at the Hospital for Special Surgery (HSS) suggests that currently available therapies may help ...

While there have been reports from drugmakers about possible interruptions with FDA matters due to staff layoffs, one company ...

Duchenne muscular dystrophy (DMD) is a fatal X-linked disorder caused by the absence of functional dystrophin, a large structural protein critical to the integrity of skeletal and cardiac muscle ...