Nasal involvement is the most commonly observed otolaryngologic feature in GPA, with symptoms often mimicking chronic rhinosinusitis. Destructive otolaryngologic manifestations in granulomatosis with ...

Two serious adverse events occurred, both of which resolved fully, and no deaths or life-threatening adverse events were reported. Prolonged treatment with tamoxifen was well tolerated in boys with ...

Key outcomes included high ILD prevalence, postmyopathic PPF in 13.5% of the cohort, higher rates of rapidly progressive ILD and transplantation in postmyopathic PPF, greater rituximab use in PPF, and ...

A qualitative matrix analysis allowed for the development of implementation strategies to improve the efficiency and effectiveness of the system. Researchers from the US identified an ideal system to ...

Life expectancy in DMD has improved over time. Previous estimates pointed to a life expectancy of 25 years, with more recent data reporting a life expectancy of 31.7 years (95% CI, 27.4-36.0). 3,4 A ...

Between 2001 to 2011, annual age-adjusted incidence increased from 0.55/100,000 to 0.78/100,000, demonstrating an increasing trend with age. Incidence peaks in individuals over 70 years of age ...

Understanding CIDP’s effects on quality of life requires attention to both typical patterns and the individual patient. Chronic inflammatory demyelinating polyneuropathy (CIDP) is a rare, ...

The authors argue that the long-held label of "uniformly lethal" may no longer be appropriate and can inadvertently bias clinical decision-making. Homozygous achondroplasia is traditionally ...

Nintedanib significantly reduced the decline in the forced vital capacity of patients with progressive pulmonary fibrosis (PPF). Treatment with nintedanib significantly slows the progression of ...